Jackson Laboratory have been busy behind the scenes conducting a safety study for the gene therapy developed to treat CdLS. 

After weeks of waiting we are are incredibly excited to reveal to all of you that believed in Hope for Hasti, that the study has shown the therapy is safe! This was a huge hurdle to have overcome and takes one huge step closer to delivering a treatment for Hasti and others with CdLS. One huge step closer to changing their lives forever. 

We can’t thank you all enough for your help and support which carried us this far.