25 Jun 20


Increasingly gene therapies are giving hope to those with genetic illness and being used to treat a wide variety of conditions, that until recently, were completely without treatment.

In 2018, a gene therapy delivered by Great Ormond Street Hospital successfully treated children with the previously fatal severe combined immunodeficiency (SCID)

In 2019, Oxford Eye Hospital have used a gene therapy to cure one of the most common forms of blindness, causing age-related macular degeneration (AMD).

Developing a successful gene therapy which can be trialled on human patients takes a huge amount of research and funding. We already have a world class research team who have started the research to create a gene therapy for Cornelia de Lange Syndrome, now all we need is the funding to keep it going and perhaps 2021 will be the year we create a gene therapy for CdLS.



Tel:  0044 79201 62569


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